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Original article
Real life experience of tafamidis for the treatment of Spanish patients with Val30Met transthyretin amyloidosis with polyneuropathy
Experiencia en vida real en España del uso de tafamidis para el tratamiento de pacientes con amiloidosis por transtirretina VAL30MET con polineuropatía
Maria Antonia Ribot Sansoa, Adrián Rodriguez Rodrigueza, Laura Martínez Vicenteb, Teresa Sevillac, Cristina Borrachero Garrod, Julian Fernández Martíne, Adrián Antón Vicentef, Moises Morales de la Pridag, Lucía Galán Dávilab, Laura González Vázquezh, Ferran Martínez Vallef, Carlos Casasnovas Ponsg,i,j, Arturo Fraga Baue, Eugenia Cisneros Barrosoa, Inés Losada Lópeza, Juan González-Morenoa,
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jgonzalez4@hsll.es

Corresponding author.
a Servicio de Medicina Interna, Unidad Amiloidosis por Trastirretina, Hospital Universitario Son Llàtzer, Instituto de Investigación Sanitaria Illes Balears (idISBA), Palma de Mallorca, Spain
b Servicio de Neurología, Unidad de Neuromuscular, IdISSC, Hospital Clínico San Carlos, Madrid, Spain
c Servicio de Neurología, Hospital Universitari i Politècnic La Fe/IISLAFE, Universitat de Valencia, CIBERER (ERN EURO-NMD), Valencia, Spain
d Servicio de Medicina Interna, UMAH, Hospital Universitario Juan Ramón Jiménez, Huelva, Spain
e Servicio de Medicina Interna, Hospital Álvaro Cunqueiro, Vigo, Spain
f Servicio de Medicina Interna, Hospital Vall d’Hebron, Barcelona, Spain
g Neuromuscular Unit, Neurology Department, Bellvitge University Hospital-IDIBELL, Spain
h Servicio de Medicina Interna, Hospital Ribera-Povisa, Vigo, Spain
i Multidisciplinary Unit of Familial Amyloidosis, Bellvitge University Hospital-IDIBELL, Neurometabolic Diseases Group, Bellvitge Biomedical Research Institute (IDIBELL), Barcelona, Spain
j Biomedical Research Network Center in Rare Diseases (CIBERER), Valencia, Spain
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ISSN: 00257753
Original language: English
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